- Community Counts - The Registry for Bleeding Disorders Surveillance Currently recruiting
- Safety and Efficacy of Nexium in Pediatric Patients with Erosive Esophagitis Currently recruiting
- Biomarkers in Tumor Samples From Patients With Newly Diagnosed Neuroblastoma or Ganglioneuroblastoma Currently recruiting
- The Project: Every Child Protocol: A Registry, Eligibility Screening, Biology and Outcome Study Currently recruiting
- Neuropsychological, Social, Emotional, and Behavioral Outcomes in Children With Cancer
- Selumetinib in Treating Young Patients With Recurrent or Refractory Low Grade Glioma Currently recruiting
- Guided Therapy in Treating Younger Patients With Non-high Risk Neuroblastoma Currently recruiting
- Maintenance Chemotherapy or Observation Following Induction Chemo and Radiation for Ependymoma Currently recruiting
- Genetic Analysis Identifying Late Occurring Complications in Childhood Cancer Survivors (ALTE03N1) Currently recruiting
- Safety and efficacy of Ravulizumab for pediatric patients with thrombocytic microangiopathy following hematopoetic stem cell transplantation Currently recruiting
- Effects of Dexrazoxane Hydrochloride on Biomarkers Associated With Cardiomyopathy and Heart Failure Currently recruiting
- Genes that influence the way your body responds to infection Currently recruiting
- Recovery after ECMO in children with Acute Respiratory Distress Syndrome Currently recruiting
- Medical device study for patients with a rare kidney disease (Focal Segmental Glomerulosclerosis) Currently recruiting
- Safety and efficacy of ASP0367 in patients with primary mitochondrial myopathy Currently recruiting
- Safety and Efficacy of REN001 in patients with Primary Mitochondrial Myopathy Currently recruiting
- Alpers Huttenlocher Natural History Study (Alpers) Currently recruiting
- Single vs. Multiple Privigen Dose Regimens in Pediatric CIDP Currently recruiting
- North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) Currently recruiting
- Safety and efficacy of Rimegepant for the treatment of migraine in pediatric patients ≥6 to <18 years of age Currently recruiting
- Assessment of reachable workspace in patients with Brachial Plexus (BP) or Cerebral Palsy (CP) Currently recruiting
- Motion Capture to Assess Function of Upper Extremities in Typically Developing Children Currently recruiting
- ROCK Prospective Cohort Study for Osteochondritis Dissecans of the Knee Currently recruiting
- Safety and efficacy of MACI in Patients with Chondral or Osteochondral Knee Defects (PEAK) Currently recruiting
- Assessment of reachable workspace in patients undergoing elbow or shoulder surgery Currently recruiting
- Prospective Database Registry of Scoliosis in Children with Cerebral Palsy Currently recruiting
- Study of Scoliosis Correction in patients with Marfan Syndrome Currently recruiting
- Pediatric Spine Registry Currently recruiting
- Prospective Database Registry of Scheuermann's Kyphosis Currently recruiting
- Scoliosis Outcomes Database Registry Currently recruiting
- Implementation of a US/Canadian Diagnostic Registry of Children with Chronic Vasculitis Currently recruiting
- The CARRA Registry for Pediatric Rheumatic Diseases Currently recruiting